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Switching from immediate- to extended-release cysteamine in patients with nephropathic cystinosis: from clinical trials to clinical practice

dc.contributor.authorAriceta, G.
dc.contributor.authorLópez Muñiz, A.
dc.contributor.authorHermida, A.
dc.contributor.authorMatoses, M. L.
dc.contributor.authorVentura, A.
dc.contributor.authorMartin Moreno, P. L.
dc.contributor.authorGonzález, E.
dc.contributor.authorAcuña, L.
dc.contributor.authorGiner, E.
dc.contributor.authorSantos Rodríguez, Fernando 
dc.contributor.authorVara, Julia
dc.date.accessioned2024-11-07T07:25:04Z
dc.date.available2024-11-07T07:25:04Z
dc.date.issued2024
dc.identifier.citationClinical Kidney Journal, 17(4), (2024); doi:10.1093/ckj/sfae049
dc.identifier.issn2048-8505
dc.identifier.urihttps://hdl.handle.net/10651/75501
dc.description.sponsorshipThe authors thank the Ethics Committee for evaluating and approving this study. We thank the participant patients and families and Grupo Cistinosis (the cystinosis patient association in Spain) for their support. This study has been funded by Chiesi España, S.A.U.
dc.language.isoeng
dc.relation.ispartofClinical Kidney Journal
dc.rights© The Author(s) 202
dc.rightsCC Reconocimiento 4.0 Internacional
dc.rights.urihttp://creativecommons.org/licenses/by/4.0/
dc.sourceScopus
dc.source.urihttps://www.scopus.com/inward/record.uri?eid=2-s2.0-85191075148&doi=10.1093%2fckj%2fsfae049&partnerID=40&md5=d556aa3df23faa01027ca05ec0768f1d
dc.titleSwitching from immediate- to extended-release cysteamine in patients with nephropathic cystinosis: from clinical trials to clinical practice
dc.typejournal article
dc.identifier.doi10.1093/ckj/sfae049
dc.relation.publisherversionhttp://dx.doi.org/10.1093/ckj/sfae049
dc.rights.accessRightsopen access


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